CRISPR Will Allow to Cure Genetic Diseases That Were Previously Incurable
The MHRA has approved Casgevy to treat sickle cell disease (SCD) and transfusion-dependent beta thalassaemia. These are lifelong genetic disorders caused by mutations in the genes that code for haemoglobin, the protein red blood cells need to transport oxygen around the body. CRISPR could treat a common form of inherited blindness. The 2020 Nobel Prize in Chemistry has gone to two women who developed a gene-editing tool called CRISPR-Cas9, which cuts DNA like molecular scissors.